---
title: "REF: Platform-based approach for AAV Gene Therapies"
slug: "ref-platform-based-approach-for-aav-gene-therapies"
updated: 2025-03-20T21:00:57Z
published: 2025-03-20T21:00:57Z
canonical: "bgtcplaybook.document360.io/ref-platform-based-approach-for-aav-gene-therapies"
---

> ## Documentation Index
> Fetch the complete documentation index at: https://bgtcplaybook.document360.io/llms.txt
> Use this file to discover all available pages before exploring further.

# REF: Platform-based approach for AAV Gene Therapies

1. Platform Technology Approach for AAV & Lenti-based Gene Therapy. ASGCT Liaison Meeting with FDA (2019) ([https://asgct.org/global/documents/advocacy/fda-liaison-meeting-2019/development-and-regulatory-considerations-when-lev.aspx](https://asgct.org/global/documents/advocacy/fda-liaison-meeting-2019/development-and-regulatory-considerations-when-lev.aspx))
2. Future of Drug Development, Janet Woodcock ([https://www.fda.gov/media/104048/download](https://www.fda.gov/media/104048/download))
3. Continuous Manufacturing of Drug Substances and Drug Products ([https://www.fda.gov/media/165775/download](https://www.fda.gov/media/165775/download))
4. The Platform Vector Gene Therapies Project: Increasing the Efficiency of Adeno-Associated Virus Gene Therapy Clinical Trial Startup. Brooks et al., (2020) ([https://www.liebertpub.com/doi/10.1089/hum.2020.259](https://www.liebertpub.com/doi/10.1089/hum.2020.259))